Trial Profile

A Phase 1/2, First-in-Human, Open-Label, Dose-Escalation Study of the Safety and Efficacy of Gene Therapy for Congenital Adrenal Hyperplasia Through Administration of an Adeno-Associated Virus (AAV) Serotype 5-Based Recombinant Vector Encoding the Human CYP21A2 Gene

Status: Active, no longer recruiting

Phase of Trial: Phase I/II

Latest Information Update: 01 Oct 2024

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At a glance

26 Sep 2024 Planned End Date changed from 1 Nov 2028 to 1 Feb 2029.
26 Sep 2024 Planned primary completion date changed from 1 Dec 2024 to 1 Feb 2029.
26 Sep 2024 Status changed from recruiting to active, no longer recruiting.

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