A Phase I Open Label Study to Evaluate the Safety and Tolerability of ISP-001 in Adult Patients With Mucopolysaccharidosis Type I Hurler-Scheie and Scheie
Latest Information Update: 24 Sep 2024
At a glance
- Drugs Iduronicrin genleukocel-T (Primary)
- Indications Mucopolysaccharidosis I
- Focus Adverse reactions; First in man
- Sponsors Immusoft
- 23 Sep 2024 According to an Immusoft media release, the company announced positive results from this trial to be presented at Immusoft's MPS I Clinical Update and Outreach webinar, on October 14, 2024.
- 23 Sep 2024 Results present in the Immusoft Media Release
- 13 Mar 2024 Planned End Date changed from 1 Oct 2024 to 1 Jun 2039.