Trial Profile

A Randomized, Double-Blind, Placebo-Controlled, Phase 1/2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Single and Multiple-Doses of AOC 1001 Administered Intravenously to Adult Myotonic Dystrophy Type 1 (DM1) Patients

Status: Completed

Phase of Trial: Phase I/II

Latest Information Update: 04 Mar 2025

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At a glance

27 Feb 2025 According to an Avidity Biosciences media release, publication of data analyses from the completed Phase 1/2 MARINA trial in 2025.
08 Jan 2025 According to an Avidity Biosciences media release, the company is planned the presentation of additional data analyses from the study in 1Q of 2025.
07 Oct 2023 New positive AOC 1001 data from this trial presented in an Avidity Biosciences media release.

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