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Expanded Access Treatment With Open-Label Pegunigalsidase Alfa for Fabry Patients

Trial Profile

Expanded Access Treatment With Open-Label Pegunigalsidase Alfa for Fabry Patients

Status: Recruiting
Phase of Trial: Clinical Phase Unknown

Latest Information Update: 03 Apr 2023

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At a glance

  • Drugs Pegunigalsidase alfa (Primary)
  • Indications Fabry's disease
  • Focus Expanded access; Therapeutic Use
  • Sponsors Chiesi Farmaceutici; Protalix Biotherapeutics
  • Most Recent Events

    • 23 Dec 2020 According to a Chiesi Global Rare Diseases media release, first patient has been enrolled in this study. This treatment was initiated by Ozlem Goker-Alpan, M.D., founder and Chief Executive Officer of the Lysosomal & Rare Disorders Research & Treatment Center (LDRTC) in Fairfax, Va, and Lauren Noll, Clinical Research Coordinator.
    • 18 Sep 2020 New trial record
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