Study of the Functional Effects of Nusinersen in 5q-spinal Muscular Amyotrophy Adults (SMA Type 2 or 3 Forms): a Multicenter Single-case Experimental Design in Multiple Baselines Across Subjects, Randomized, Single-blinded Evaluation
Latest Information Update: 06 Dec 2024
At a glance
- Drugs Nusinersen (Primary)
- Indications Spinal muscular atrophy
- Focus Therapeutic Use
- Acronyms NUSI-AD-5qSM
Most Recent Events
- 02 Dec 2024 Status changed from recruiting to completed.
- 16 Mar 2022 Planned End Date changed from 1 May 2024 to 1 Jun 2025.
- 16 Mar 2022 Planned primary completion date changed from 1 Dec 2021 to 24 Jan 2023.