A Phase 1/2 Safety, Tolerability, and Efficacy Study of BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in Hemophilia A Patients With Active or Prior Inhibitors
Latest Information Update: 25 Sep 2024
Price :
$35 *
At a glance
- Drugs Valoctocogene-roxaparvovec (Primary)
- Indications Haemophilia A
- Focus Adverse reactions
- Acronyms GENEr8-INH
- Sponsors BioMarin Pharmaceutical
- 25 Sep 2024 This trial has been discontinued in Italy, according to European Clinical Trials Database record.
- 05 Jul 2024 Planned End Date changed from 1 Feb 2029 to 1 Apr 2029.
- 05 Jul 2024 Planned primary completion date changed from 1 Feb 2029 to 1 Apr 2029.