A compassionate program study in immune-mediated thrombotic thrombocytopenic purpura patients assessing response to daily therapeutic plasma exchange, steroids and caplacizumab
Latest Information Update: 10 Nov 2020
At a glance
- Drugs Caplacizumab (Primary) ; Caplacizumab (Primary) ; Prednisone (Primary) ; Rituximab (Primary) ; Bortezomib; Corticosteroids; Cyclophosphamide; Vincristine
- Indications Thrombotic thrombocytopenic purpura
- Focus Expanded access; Therapeutic Use
Most Recent Events
- 10 Nov 2020 New trial record
- 04 Nov 2020 Primary endpoint (Composite of refractoriness and death within 30 days since diagnosis) has been met, according to results published in the Blood
- 04 Nov 2020 Results published in the Blood