Symptoms of nonsense mutation duchenne muscular dystrophy and its impact on health-related quality of life
Latest Information Update: 24 Nov 2020
At a glance
- Drugs Ataluren (Primary)
- Indications Duchenne muscular dystrophy
- Focus Therapeutic Use
Most Recent Events
- 24 Nov 2020 New trial record
- 19 Nov 2020 Results assessing symptoms and impacts of nonsense mutation DMD (nmDMD) at different stages of ambulation, presented at the 23rd Annual European Congress of the International Society for Pharmacoeconomics and Outcomes Research
- 19 Nov 2020 Results presented at the 23rd Annual European Congress of the International Society for Pharmacoeconomics and Outcomes Research