A Phase I/II, Open Label, Single Dose Clinical Study to Evaluate the Safety and Therapeutic Effects of Transplantation of MNV-BM-BLD (Autologous cd34+ Cells Enriched With Blood Derived Mitochondria) in Pediatric Patients With Pearson Syndrome
Latest Information Update: 06 Oct 2021
At a glance
- Drugs MNV-BLD (Primary)
- Indications VLCAD deficiency
- Focus Adverse reactions; Expanded access; Therapeutic Use
- Sponsors Minovia Therapeutics
- 01 Oct 2021 According to a Minovia therapeutics media release, Toren, of the division of pediatric hematology and oncology, is lead Principal Investigator of this study.
- 30 Aug 2021 Status changed from recruiting to completed.
- 12 Mar 2021 According to a Minovia therapeutics media release, twelve patients have been dosed so far in Israel in this study.