An Intermediate Size Expanded Access Protocol of Elamipretide for Subcutaneous Injection in Patients With Genetically Confirmed Rare Diseases With Known Mitochondrial Dysfunction
Latest Information Update: 15 Jul 2024
At a glance
- Drugs Elamipretide (Primary)
- Indications Barth syndrome; Cardiomyopathies; Corneal disorders; Diabetic macular oedema; Dry age-related macular degeneration; Friedreich's ataxia; Heart failure; Leber's hereditary optic atrophy; Mitochondrial disorders; Mitochondrial myopathies; Renal impairment
- Focus Expanded access; Therapeutic Use
- Sponsors Stealth BioTherapeutics
- 04 Jan 2021 New trial record