An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome
Latest Information Update: 04 Feb 2025
At a glance
- Drugs NNZ 2591 (Primary)
- Indications Angelman syndrome
- Focus Adverse reactions; Pharmacokinetics
- Acronyms AS-001
- Sponsors Neuren Pharmaceuticals
Most Recent Events
- 07 Aug 2024 Status changed from active, no longer recruiting to completed.
- 20 Dec 2023 According to a Neuren Pharmaceuticals media release, company announced that the last subject to be screened this week will complete the enrolment of subjects in this trial.
- 20 Dec 2023 According to a Neuren Pharmaceuticals media release, top-line results from the trial are expected to be available in Q3 2024.