An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Pitt Hopkins Syndrome (PTHS-001)
Latest Information Update: 25 Feb 2025
At a glance
- Drugs NNZ 2591 (Primary)
- Indications Pitt-Hopkins syndrome
- Focus Adverse reactions; Pharmacokinetics
- Acronyms PTHS-001
- Sponsors Neuren Pharmaceuticals
- 22 Jan 2025 According to a Neuren Pharmaceuticals media release, company will present data at the 2025 American College of Medical Genetics and Genomics (ACMG) Annual Clinical Genetics Meeting, being held on 18-22 March 2025, in Los Angeles.
- 08 Aug 2024 Status changed from active, no longer recruiting to completed.
- 27 May 2024 Results published in the Neuren Pharmaceuticals Media Release