Randomized, double-blind, placebo-controlled, multicenter clinical trial of CARBAGLU for the treatment of hyperammonemic episodes in patients with propionic academia or methylmalonic academia
Latest Information Update: 04 Feb 2021
At a glance
- Drugs Carglumic acid (Primary)
- Indications Methylmalonic acidaemia; Propionic acidaemia
- Focus Therapeutic Use
Most Recent Events
- 04 Feb 2021 Planned number of patients changed from 24 to NULL.
- 04 Feb 2021 New trial record
- 26 Jan 2021 Results presented in the Recordati Rare Diseases Media Release.