Trial Profile

A clinical study of CLN3 Batten disease gene therapy program, AT-GTX-502

Status: Planning

Phase of Trial: Phase II

Latest Information Update: 11 Feb 2021

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At a glance

Drugs AAV9 CLN3 (Primary)
Indications Neuronal ceroid lipofuscinosis
Focus Therapeutic Use
Sponsors Amicus Therapeutics

Most Recent Events

11 Feb 2021 New trial record
08 Feb 2021 According to the Amicus Therapeutics media release, IND is planned to be submitted for this study in 2H2021.

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