A Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Safety and Efficacy of Crinecerfont (NBI-74788) in Pediatric Subjects With Classic Congenital Adrenal Hyperplasia, Followed by Open-Label Treatment
Latest Information Update: 08 Jul 2026
At a glance
- Drugs Crinecerfont (Primary)
- Indications Congenital adrenal hyperplasia
- Focus Registrational; Therapeutic Use
- Acronyms CAHtalyst Pediatric Study
- Sponsors Neurocrine Biosciences
Most Recent Events
- 08 Jul 2026 Last checked against Clinical Trials Information System record.
- 15 Jun 2026 According to a Neurocrine Biosciences media release, data from the trial were presented at the Endocrine Society's annual meeting, ENDO 2026, in Chicago.
- 15 Jun 2026 Results presented in the Neurocrine Biosciences Media Release