Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

A Phase1/2a Dose-Escalating Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ARO-DUX4 in Adult Patients With Facioscapulohumeral Muscular Dystrophy Type 1

Next Previous
Trial Profile

A Phase1/2a Dose-Escalating Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ARO-DUX4 in Adult Patients With Facioscapulohumeral Muscular Dystrophy Type 1

Status: Recruiting
Phase of Trial: Phase I/II

Latest Information Update: 21 Aug 2026

Price :
$35 *
Note:
  • Adis is an information provider.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our trial profile at the time of purchase.
  • A link to download a PDF version of the trial profile will be included in your email receipt.

At a glance

  • Drugs SRP 1001 (Primary) ; Sodium chloride
  • Indications Facioscapulohumeral muscular dystrophy
  • Focus Adverse reactions; First in man
  • Sponsors Arrowhead Pharmaceuticals; Sarepta Therapeutics

Most Recent Events

  • 11 Aug 2026 Planned End Date changed from 1 Dec 2026 to 31 Dec 2028.
  • 11 Aug 2026 Planned primary completion date changed from 1 Dec 2026 to 31 Dec 2028.
  • 05 Aug 2026 According to a Sarepta Therapeutics media release, readouts from MAD cohort remain on track for 2H 2026.

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top