A Prospective Observational Study to Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)

Status: Recruiting

Phase of Trial: Phase IV

Latest Information Update: 29 Jul 2024

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15 Dec 2023 Planned End Date changed from 11 Apr 2025 to 30 Mar 2026.
15 Dec 2023 Planned primary completion date changed from 11 Apr 2025 to 30 Mar 2026.
12 Dec 2022 Planned End Date changed from 12 Nov 2024 to 11 Apr 2025.

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