Trial Profile

An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome

Status: Discontinued

Phase of Trial: Phase II/III

Latest Information Update: 07 Mar 2025

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At a glance

Drugs Trofinetide (Primary)
Indications Rett syndrome
Focus Adverse reactions; Pharmacokinetics
Acronyms DAFFODIL
Sponsors Acadia Pharmaceuticals

Most Recent Events

05 Mar 2025 Results presented in an Acadia Pharmaceuticals Media Release.
05 Mar 2025 According to an Acadia Pharmaceuticals media release, results of DAFFODIL, LAVENDER, LILAC-1 and LILAC-2 studies supported the FDA approval of DAYBUE in adults and pediatric patients two years of age or older.
05 Mar 2025 According to an Acadia Pharmaceuticals media release, results of this study published in the journal Med.

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