Treatment of beta-thalassemia patients with rapamycin (sirolimus): from pre-clinical research to a clinical trial Trattamento di pazienti con beta-talassemia con Rapamicina (sirolimus): dalla ricerca pre-clinica ad uno studio clinico
Latest Information Update: 20 Aug 2021
At a glance
- Drugs Sirolimus (Primary)
- Indications Beta-thalassaemia
- Focus Therapeutic Use
- Acronyms THALA-RAP
- 20 Aug 2021 New trial record