A Multicenter, Randomized, Controlled, Open-label, Rater-blinded Study to Evaluate Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of ALXN1840 Versus Standard of Care in Pediatric Participants With Wilson Disease
Latest Information Update: 20 Apr 2026
At a glance
- Drugs Tiomolibdate choline (Primary)
- Indications Hepatolenticular degeneration
- Focus Registrational; Therapeutic Use
- Sponsors Alexion AstraZeneca Rare Disease
Most Recent Events
- 27 Mar 2026 According to Monopar media release, the company plans to submit NDA for ALXN1840 for Wilson Disease in mid-2026.
- 31 Aug 2023 This Trial has been completed in Poland according to European Clinical Trials Database record.
- 11 Jul 2023 Status changed from active, no longer recruiting to discontinued.