A Randomized, Placebo-Controlled, Multiple Ascending Dose Study Assessing Safety, Tolerability, Pharmacodynamics, Efficacy, and Pharmacokinetics of DYNE-101 Administered to Participants With Myotonic Dystrophy Type 1
Latest Information Update: 16 Oct 2024
At a glance
- Drugs DYNE-101 (Primary)
- Indications Myotonic dystrophy
- Focus Adverse reactions; First in man; Registrational
- Acronyms ACHIEVE
- Sponsors Dyne Therapeutics
- 09 Oct 2024 Results presented in the Dyne Therapeutics Media Release.
- 09 Oct 2024 According to a Dyne Therapeutics media release, data from this trial will be presented at the 29th Annual Congress of the World Muscle Society, held virtually and in Prague, Czech Republic, October 8-12, 2024.
- 26 Sep 2024 Planned number of patients changed from 96 to 104.