Trial Profile

A Randomized, Double-Blind, Placebo-Controlled, Multiple Ascending Dose Study Assessing Safety, Tolerability, Pharmacodynamics, Efficacy, and Pharmacokinetics of DYNE-251 Administered to Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping

Status: Active, no longer recruiting

Phase of Trial: Phase I/II

Latest Information Update: 17 Dec 2025

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At a glance

08 Dec 2025 According to a Dyne Therapeutics media release, company will host a conference call and webcast to discuss these updates, December 8, 2025, at 8:00 a.m.
08 Dec 2025 According to a Dyne Therapeutics media release,the company is on track to submit for U.S. Accelerated Approval in Q2 2026, positioning us for a potential Q1 2027 launch.
08 Dec 2025 Primary endpoint (A registrational expansion cohort:) has been met.

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