Trial Profile

A 2-part Phase 2 Study of Safety, Pharmacokinetics and Biomarkers in Children With Duchenne Muscular Dystrophy Including a Randomized, Double-Blind, Placebo-Controlled Part A, Followed by an Open-Label Part B

Status: Active, no longer recruiting

Phase of Trial: Phase II

Latest Information Update: 15 May 2025

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At a glance

08 May 2025 According to an Edgewise Therapeutics media release, the company is on track to report data from this study in 2Q 2025.
13 Jan 2025 According to an Edgewise Therapeutics media release, data from the study expected in in the first half of 2025.
27 Dec 2024 Status changed from recruiting to active, no longer recruiting.

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