Tetrahydrobiopterin (BH4) treatment in Phenylketonuria - comparing different practices of dosing regimen
Latest Information Update: 30 Nov 2021
At a glance
- Drugs Sapropterin (Primary)
- Indications Phenylketonuria
- Focus Pharmacokinetics
- Acronyms BH4 dose
- 30 Nov 2021 New trial record