Trial Profile

A French Multicenter Open Label Phase 4 Extension Study of Long-term Safety and Efficacy in Patients With Pompe Disease Who Previously Participated in Avalglucosidase Alfa Development Studies in France

Status: Active, no longer recruiting

Phase of Trial: Phase IV

Latest Information Update: 16 Sep 2026

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At a glance

09 Sep 2026 Planned End Date changed from 30 Sep 2026 to 30 Jun 2027.
09 Sep 2026 Planned primary completion date changed from 30 Sep 2026 to 30 Jun 2027.
29 Jul 2026 Planned number of patients changed from 18 to 17.

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