A retrospective study assessing the airway abnormalities and pulmonary complications in long-term Myozyme treated late-onset Pompe disease
Latest Information Update: 18 Jan 2022
At a glance
- Drugs Alglucosidase alfa (Primary)
- Indications Glycogen storage disease type II
- Focus Therapeutic Use
Most Recent Events
- 18 Jan 2022 New trial record
- 01 Jan 2022 Results published in the Pediatric Pulmonology