Multicenter, Open-Label, Multi-cohort Study to Evaluate Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Drug Product GNR 055 (JSC "GENERIUM", Russia) in Patients With Mucopolysaccharidosis Type II
Latest Information Update: 27 Feb 2023
At a glance
- Drugs GNR 055 (Primary)
- Indications Mucopolysaccharidosis II
- Focus Adverse reactions; Pharmacokinetics
- Sponsors GENERIUM Pharmaceuticals
Most Recent Events
- 22 Feb 2023 Planned End Date changed from 1 Mar 2025 to 1 Mar 2028.
- 02 Feb 2022 New trial record