Trial Profile

An Open-Label, Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease

Status: Active, no longer recruiting

Phase of Trial: Phase III

Latest Information Update: 06 Mar 2025

Price :

$35 ^*

Note:

Adis is an information provider.
Final gross price and currency may vary according to local VAT and billing address.
Your purchase entitles you to full access to the information contained in our trial profile at the time of purchase.
A link to download a PDF version of the trial profile will be included in your email receipt.

At a glance

Drugs Vatiquinone (Primary)
Indications Lactic acidosis; Leigh disease; MELAS syndrome; MERRF syndrome; Mitochondrial disorders; Mitochondrial encephalomyopathies; Olivopontocerebellar atrophies
Focus Adverse reactions; Registrational
Sponsors PTC Therapeutics

Most Recent Events

04 Mar 2025 Status changed from recruiting to active, no longer recruiting.
23 Sep 2024 Planned number of patients changed from 100 to 204.
23 Sep 2024 This trial has been Discontinued in Sweden, according to European Clinical Trials Database.

You need to be a logged in or subscribed to view this content

If your organization or you do not have a subscription, try one of the following:

Contacting your organization’s admin about adding this content to your AdisInsight subscription
Buying a PDF version of any individual profile
Request a free trial (opens in a new window)

If your organization has a subscription, there are several access options, even while working remotely:

Working within your organization’s network
Login with username/password or try to access via your institution
Persisted access using your organization’s identifier stored in your user browser for 90 days

For assistance, contact us at asktheexpert.adisinsight@springer.com