A UT Southwestern-Sponsored first-in-human, single center, open-label, dose escalation study of Neuronal ceroid lipofuscinosis gene therapy for the treatment of CLN7 Batten disease
Latest Information Update: 23 May 2022
At a glance
- Drugs Neuronal ceroid lipofuscinosis gene therapy-University of Texas Southwestern Medical Center (Primary)
- Indications Neuronal ceroid lipofuscinosis
- Focus Adverse reactions; First in man
Most Recent Events
- 16 May 2022 According to a Taysha Gene Therapies media release, fourth patient with CLN7 disease dosed at 1.0 x 1015 total vg.
- 14 Feb 2022 New trial record
- 09 Feb 2022 According to a Taysha Gene Therapies media release, this trial is enrolling patients at Childrens Health.