Trial Profile

A Phase 3 Study to Evaluate the Safety and Efficacy of a Single Dose of CTX001 in Pediatric Subjects With Transfusion-Dependent ß-Thalassemia

Status: Active, no longer recruiting

Phase of Trial: Phase III

Latest Information Update: 21 Oct 2024

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At a glance

Drugs Exagamglogene autotemcel (Primary) ; Busulfan; Filgrastim; Plerixafor
Indications Beta-thalassaemia
Focus Registrational; Therapeutic Use
Acronyms CLIMB-141
Sponsors Vertex Pharmaceuticals

Most Recent Events

01 Aug 2024 This trial has been suspended in Germany, according to European Clinical Trials Database.
06 Jun 2024 This trial is ongoing in Germany According to against European Clinical Trials Database record.
10 May 2024 This trial has been suspended in Germany.

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