Trial Profile

Open-label, Dose-escalation, Phase 1 Clinical Trial to Determine the Safety and Dose of EN001 in Patients With Charcot-Marie-Tooth Disease (CMT) Type 1A

Status: Completed

Phase of Trial: Phase I

Latest Information Update: 17 Mar 2025

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At a glance

Drugs EN 001 (Primary)
Indications Charcot-Marie-Tooth disease
Focus Adverse reactions; First in man
Sponsors ENCell

Most Recent Events

03 Mar 2025 Results presented in an ENCell Media Release.
26 Jun 2024 According to ENCell media release, data from the study were presented at the Peripheral Nerve Society (PNS) annual meeting in Montreal on June 23, 2024.
26 Jun 2024 Results presented in the ENCell Media Release.

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