A real world study to assess effects of voretigene neparvovec treatment in pediatric patients with RPE65-associated Leber congenital amaurosis
Latest Information Update: 09 May 2022
At a glance
- Drugs Voretigene neparvovec (Primary)
- Indications Leber congenital amaurosis
- Focus Therapeutic Use
Most Recent Events
- 09 May 2022 New trial record
- 01 May 2022 Results published in the Graefes Archive for Clinical and Experimental Ophthalmology