To determine whether deflazacort is non-inferior to 0.9 mg/kg/d among newly diagnosed patients with Duchenne muscular dystrophy
Latest Information Update: 14 Jun 2022
At a glance
- Drugs Deflazacort (Primary)
- Indications Duchenne muscular dystrophy
- Focus Therapeutic Use
- Acronyms DOSE
- 14 Jun 2022 New trial record
- 01 May 2022 Primary endpoint (change in 6MWD, from baseline to week-24 of intervention) has not been met according to the results published in the European Journal of Paediatric Neurology
- 01 May 2022 Results published in the European Journal of Paediatric Neurology