A PHASE 2, MULTICENTER, SINGLE-ARM STUDY TO EVALUATE THE SAFETY AND DYSTROPHIN EXPRESSION AFTER FORDADISTROGENE MOVAPARVOVEC (PF-06939926) ADMINISTRATION IN MALE PARTICIPANTS WITH EARLY STAGE DUCHENNE MUSCULAR DYSTROPHY
Latest Information Update: 05 Sep 2025
At a glance
- Drugs Fordadistrogene-movaparvovec (Primary)
- Indications Duchenne muscular dystrophy
- Focus Adverse reactions
- Sponsors Pfizer
Most Recent Events
- 09 Jul 2025 Planned End Date changed from 30 Jun 2025 to 19 Sep 2025.
- 09 Jul 2025 Planned primary completion date changed from 30 Jun 2025 to 19 Sep 2025.
- 18 Apr 2025 Planned End Date changed from 3 Jan 2029 to 30 Jun 2025.