An open-label, single-center study on the safety and efficacy of avalglucosidase alpha in late-onset Pompe patients ≥5 years
Latest Information Update: 28 Jun 2022
At a glance
- Drugs Avalglucosidase alfa (Primary)
- Indications Glycogen storage disease type II
- Focus Therapeutic Use
- Acronyms AVA
Most Recent Events
- 28 Jun 2022 New trial record