Phase I/II Study Using Allogeneic Hematopoietic Stem Cell Transplantation for Chronic Granulomatous Disease With an Alemtuzumab, Busulfan and TBI-based Conditioning Regimen Combined With Cytokine (IL-6, +/- IFN-gamma) Antagonists
Latest Information Update: 17 Jul 2024
At a glance
- Drugs Alemtuzumab (Primary) ; Busulfan (Primary) ; Cyclophosphamide (Primary) ; Emapalumab (Primary) ; Sirolimus (Primary) ; Tocilizumab (Primary) ; Stem cell therapies
- Indications Chronic granulomatous disease
- Focus Therapeutic Use
Most Recent Events
- 23 Jul 2022 New trial record