Trial Profile

A Phase 2 Extension Study to Evaluate the Long-Term Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of AOC 1001 Administered Intravenously to Adult Myotonic Dystrophy Type 1 (DM1) Patients

Status: Active, no longer recruiting

Phase of Trial: Phase II

Latest Information Update: 15 Jan 2025

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At a glance

08 Jan 2025 According to an Avidity Biosciences media release, the company planned the update from this trial including long-term 4mg/kg and safety data in the 4Q of 2025.
25 Jun 2024 Time frame for primary outcome increased from up to Day 729 to up to Week 208.
25 Jun 2024 Planned End Date changed from 1 Jun 2025 to 1 Jun 2027.

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