A clinical trial evaluating effect of sodium phenylbutyrate in acute management of MSUD attacks; a single-center experience
Latest Information Update: 04 Aug 2022
At a glance
- Drugs Sodium phenylbutyrate (Primary)
- Indications Maple syrup urine disease
- Focus Therapeutic Use
Most Recent Events
- 04 Aug 2022 New trial record
- 01 Nov 2020 Results published in the Journal of Pediatric Endocrinology and Metabolism