Open-Label Multicenter Extension Study to Further Evaluate Safety, Tolerability and Efficacy of Intracerebroventricular AX 250 Treatment in Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) Patients
Latest Information Update: 30 Jan 2024
Price :
$35 *
At a glance
- Drugs Tralesinidase alfa (Primary)
- Indications Mucopolysaccharidosis III
- Focus Registrational; Therapeutic Use
- Sponsors Allievex Corporation
- 16 Dec 2023 This trial has been suspended in Germany according to European Clinical Trials Database record.
- 16 Jan 2023 Status changed from not yet recruiting to recruiting.
- 11 Aug 2022 New trial record