Trial Profile

A Phase 3, Parallel-Group Treatment, Blinded, Randomized, Placebo-Controlled Study To Assess The Efficacy And Safety Of Pegtibatinase Administered Subcutaneously In Addition To Standard Of Care In Participants With Classical Homocystinuria Due To Cystathionine Beta Synthase Deficiency (HARMONY).

Status: Active, no longer recruiting

Phase of Trial: Phase III

Latest Information Update: 18 May 2026

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At a glance

04 May 2026 According to a Travere Therapeutics media release, in April 2026 first new patient dosed in the restarted Phase 3 HARMONY study and topline data expected 2H 2027.
20 Feb 2025 According to a Travere Therapeutics media release, company is on track to restart enrollment in the Phase 3 HARMONY Study in 2026.
26 Sep 2024 event According to a Travere Therapeutics media release, status changed from recruiting to active, no longer recruiting.

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