Retrospective Cohort Study to Investigate the Safety and Efficacy of Chenodeoxycholic Acid (CDCA) in Patients Affected by Cerebrotendinous Xanthomatosis (CTX)
Latest Information Update: 18 Aug 2022
At a glance
- Drugs Chenodeoxycholic acid (Primary)
- Indications Cerebrotendinous xanthomatosis
- Focus Therapeutic Use
- Sponsors Leadiant Biosciences
- 18 Aug 2022 New trial record