Mechanisms and Treatment of Exercise Intolerance and Persistent Fatigue in SMA
Latest Information Update: 26 Sep 2024
At a glance
- Drugs Nusinersen (Primary) ; Risdiplam (Primary)
- Indications Spinal muscular atrophy
- Focus Therapeutic Use
Most Recent Events
- 15 Dec 2022 Status changed from not yet recruiting to recruiting.
- 12 Sep 2022 New trial record