Expanded Access Program for Tiratricol in Patients with Monocarboxylate Transporter 8 Deficiency Also Known As Allan-Herndon-Dudley Syndrome (AHDS)
Latest Information Update: 15 Jan 2025
At a glance
- Drugs Tiratricol (Primary)
- Indications Allan-Herndon-Dudley syndrome
- Focus Expanded access; Therapeutic Use
- Sponsors Egetis Therapeutics
- 13 Dec 2023 According to an Egetis Therapeutics media release, the company has partnered with AnovoRx to optimize the execution of and further broaden the outreach and implementation of the EAP for more than 50 additional MCT8 deficiency patients in the USA.
- 09 Jun 2023 Status changed from planning to recruiting.
- 26 Apr 2023 According to an Egetis Therapeutics media release, On the request of the FDA Egetis submitted in the fourth quarter of 2022 an Expanded Access Program in the USA.