A Phase 2, Randomised, Double-blind, Placebo-controlled, 2-way Crossover Study to Evaluate the Efficacy, Safety, and Tolerability of NMD670 in Ambulatory Adults With Type 3 Spinal Muscular Atrophy
Latest Information Update: 18 Mar 2025
At a glance
- Drugs Bromophenoxyazole propanoic acid (Primary)
- Indications Spinal muscular atrophy
- Focus Proof of concept; Therapeutic Use
- Acronyms SYNAPSE-SMA
- Sponsors NMD Pharma
Most Recent Events
- 13 Mar 2025 Planned End Date changed from 1 Jul 2025 to 1 Jan 2026.
- 13 Mar 2025 Planned primary completion date changed from 1 Jul 2025 to 1 Jan 2026.
- 06 Jan 2025 According to a NMD Pharma media release, the company has three ongoing global clinical trials investigating NMD670 including a Phase 2 study in adults living with spinal muscular atrophy (SMA) type 3, a Phase 2b study in gMG patients, and this Phase 2 CMT study, with data readout(s) occurring from 2H/2025 through 1H/2026.