A Phase 1/2, Multi-regional, Single-Arm, Open-Label, Dose-Finding Clinical Trial to Evaluate the Safety, Tolerability and Efficacy of Gene Therapy for Leber's Hereditary Optic Neuropathy (LHON) Associated With ND1 Mutation

Status: Discontinued

Phase of Trial: Phase I/II

Latest Information Update: 30 Sep 2024

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At a glance

Drugs NFS 02 (Primary)
Indications Leber's hereditary optic atrophy
Focus Adverse reactions
Sponsors Neurophth Therapeutics

Most Recent Events

20 Sep 2024 Status changed from recruiting to discontinued.
06 Sep 2023 According to a Neurophth Therapeutics media release, study has enrolled and administered medication to the first patient in its international multi-center Phase I/II clinical trials in both the US and China.
17 Aug 2023 Status changed from not yet recruiting to recruiting, according to a Neurophth Therapeutics media release.

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