Trial Profile

A Phase 1 Dose Escalation Trial Evaluating an Intravenously Administered Recombinant Adeno-Associated Virus Serotype rh.74 (AAVrh.74) Vector Containing the Human Plakophilin-2a (PKP2a) Coding Sequence (RP-A601; AAVrh.74-PKP2a) in Subjects With Arrhythmogenic Cardiomyopathy Arising From Pathogenic PKP2 Variants (PKP2-ACM)

Status: Recruiting

Phase of Trial: Phase I

Latest Information Update: 21 May 2025

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At a glance

15 May 2025 According to a Rocket Pharmaceuticals media release, results of this study were presented at the Annual Meeting of the American Society of Gene and Cell Therapy (ASGCT) and will be discussed on a company webinar today at 4:30 p.m. ET.
15 May 2025 Preliminary results presented in a Rocket Pharmaceuticals Media Release.
09 May 2025 According to a Rocket Pharmaceuticals media release, Rocket plans to host an investor webinar on May 15, 2025, at 4:30 p.m. ET.

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