Trial Profile

Clinical study of RP-A501 for Danon Disease in female

Status: Planning

Phase of Trial: Phase II

Latest Information Update: 12 Jan 2023

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At a glance

Drugs RP A501 (Primary)
Indications Glycogen storage disease type II
Focus Therapeutic Use

Most Recent Events

12 Jan 2023 New trial record
09 Jan 2023 According to a Rocket Pharmaceuticals media release, the company expect to initiate this trial in Q4 2023.

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