A study evaluating clinical experience of adults with SMA treated with risdiplam through the Early Access to Medicines Scheme (EAMS) in Northern Ireland
Latest Information Update: 06 Feb 2023
At a glance
- Drugs Risdiplam (Primary)
- Indications Spinal muscular atrophy
- Focus Therapeutic Use
Most Recent Events
- 06 Feb 2023 New trial record
- 01 Feb 2023 Results published in the Muscle and Nerve