An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB
Latest Information Update: 07 Feb 2025
At a glance
- Drugs JR-446 (Primary)
- Indications Mucopolysaccharidosis III
- Focus Adverse reactions; Therapeutic Use
- Sponsors JCR Pharmaceuticals
Most Recent Events
- 03 Feb 2025 Planned End Date changed from 30 Sep 2029 to 5 Dec 2028.
- 03 Feb 2025 Planned primary completion date changed from 31 Mar 2027 to 5 Jun 2026.
- 05 Dec 2024 According to a JCR Pharmaceuticals media release, Dr. Motomichi Kosuga, Medical Director of the Division of Medical Genetics, National Center for Child Health and Development, is the Medical Expert of the study.