An Open, Dose-escalating Early Clinical Trial to Evaluate the Tolerability, Safety, and Efficacy of VGN-R09b by Intra Striatum Injection in Patients With Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.
Latest Information Update: 17 Mar 2023
At a glance
- Drugs VGN-R09 (Primary)
- Indications Aromatic amino acid decarboxylase deficiency
- Focus Adverse reactions; Therapeutic Use
Most Recent Events
- 17 Mar 2023 New trial record